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Kliniska studier för Adrenoleukodystrofi i Pennsylvania

4 studier för Adrenoleukodystrofi söker deltagare vid platser i Pennsylvania.

Städer i Pennsylvania

Officiell studietext (engelska)

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarObservationsstudie
2 Months – 60 Years · Alla kön · Uppdaterad 13 jan. 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarFas 2
2 Months – 55 Years · Alla kön · Uppdaterad 15 dec. 2025 · NCT01962415

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 23 okt. 2025 · NCT03047369

A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel

  • Children's Hospital of Philadelphia, Philadelphia
RekryterarObservationsstudie
Alla åldrar · Män · Uppdaterad 2 juli 2025 · NCT06224413

Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.