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Kliniska studier för Adrenoleukodystrofi i Pennsylvania
4 studier för Adrenoleukodystrofi söker deltagare vid platser i Pennsylvania.
Städer i Pennsylvania
Officiell studietext (engelska)
Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarObservationsstudie
2 Months – 60 Years · Alla kön · Uppdaterad 13 jan. 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarFas 2
2 Months – 55 Years · Alla kön · Uppdaterad 15 dec. 2025 · NCT01962415The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 23 okt. 2025 · NCT03047369A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel
- Children's Hospital of Philadelphia, Philadelphia
RekryterarObservationsstudie
Alla åldrar · Män · Uppdaterad 2 juli 2025 · NCT06224413Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.