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Kliniska studier för Beta-talassemi i Pennsylvania
5 studier för Beta-talassemi söker deltagare vid platser i Pennsylvania.
Städer i Pennsylvania
Officiell studietext (engelska)
ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia
- Children's Hospital of Philadelphia, Philadelphia
RekryterarFas 1/2
Ålder 18 till 40 · Alla kön · Uppdaterad 23 sep. 2026 · NCT06364774T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias
- Children's Hospital of Pittsburgh of UPMC, Pittsburgh
RekryterarFas 1/2
Ålder 5 till 40 · Alla kön · Uppdaterad 13 aug. 2026 · NCT03653338Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarObservationsstudie
2 Months – 60 Years · Alla kön · Uppdaterad 13 jan. 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarFas 2
2 Months – 55 Years · Alla kön · Uppdaterad 15 dec. 2025 · NCT01962415A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel
- Children's Hospital of Philadelphia, Philadelphia
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 11 feb. 2025 · NCT06271512Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.