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Kliniska studier för Gauchers sjukdom i Pennsylvania
5 studier för Gauchers sjukdom söker deltagare vid platser i Pennsylvania.
Städer i Pennsylvania
Officiell studietext (engelska)
A Gaucher Disease Gene Therapy Trial With FLT201
- Children's Hospital of Philadelphia, Philadelphia
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarFas 3
Ålder 18 och äldre · Alla kön · Uppdaterad 3 sep. 2026 · NCT07223944International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
- Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
- och 1 fler
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 14 apr. 2026 · NCT00358943Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 9 feb. 2026 · NCT03333200Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarObservationsstudie
2 Months – 60 Years · Alla kön · Uppdaterad 13 jan. 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekryterarFas 2
2 Months – 55 Years · Alla kön · Uppdaterad 15 dec. 2025 · NCT01962415Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.