Hem › Spinal muskelatrofi › Arkansas
Kliniska studier för Spinal muskelatrofi i Arkansas
4 studier för Spinal muskelatrofi söker deltagare vid platser i Arkansas.
Städer i Arkansas
Officiell studietext (engelska)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 2 okt. 2026 · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Arkansas Children's Hospital, Little Rock
RekryterarFas 2
Ålder 5 till 17 · Alla kön · Uppdaterad 14 sep. 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 10 sep. 2026 · NCT05861999Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Arkansas Children's Hospital, Little Rock
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 31 jan. 2025 · NCT04174157Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.