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Kliniska studier för Spinal muskelatrofi i Arkansas

4 studier för Spinal muskelatrofi söker deltagare vid platser i Arkansas.

Städer i Arkansas

Officiell studietext (engelska)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • University of Arkansas for Medical Sciences, Little Rock
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 2 okt. 2026 · NCT05861986

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • University of Arkansas for Medical Sciences, Little Rock
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 10 sep. 2026 · NCT05861999

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Arkansas Children's Hospital, Little Rock
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 31 jan. 2025 · NCT04174157

Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.