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Kliniska studier för Spinal muskelatrofi i Georgia
3 studier för Spinal muskelatrofi söker deltagare vid platser i Georgia.
Städer i Georgia
Officiell studietext (engelska)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 2 okt. 2026 · NCT05861986A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- Children's Healthcare of Atlanta, Atlanta
RekryterarFas 2
Upp till ålder 2 · Alla kön · Uppdaterad 2 okt. 2026 · NCT07047144A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 10 sep. 2026 · NCT05861999Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.