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Kliniska studier för Spinal muskelatrofi i Pennsylvania
8 studier för Spinal muskelatrofi söker deltagare vid platser i Pennsylvania.
Städer i Pennsylvania
Officiell studietext (engelska)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Children'S Hospital of Philadelphia, Philadelphia
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 2 okt. 2026 · NCT05861986A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- The Children's Hospital of Philadelphia, Philadelphia
RekryterarFas 2
Upp till ålder 2 · Alla kön · Uppdaterad 2 okt. 2026 · NCT07047144A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Children's Hospital Philadelphia - Neurology, Philadelphia
RekryterarFas 2
Ålder 5 till 17 · Alla kön · Uppdaterad 14 sep. 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Children'S Hospital of Philadelphia, Philadelphia
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 10 sep. 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Milton S. Hershey Medical Center | Pennsylvania State University_Hershey, Hershey
- Children's Hospital of Philadelphia, Philadelphia
RekryterarFas 1
Ålder 3 och äldre · Alla kön · Uppdaterad 3 sep. 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Penn State Milton S. Hershey Medical Center, Hershey
- Children's Hospital Philadelphia, Philadelphia
Rekryterar
Ålder 3 och äldre · Alla kön · Uppdaterad 19 aug. 2026 · NCT05866419ALS/MND Natural History Study Data Repository
- Thomas Jefferson University, Philadelphia
- Temple University Lewis Katz School of Medicine, Philadelphia
- University of Pittsburgh, Pittsburgh
RekryterarObservationsstudie
Ålder 18 till 90 · Alla kön · Uppdaterad 20 maj 2026 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Penn State Hershey, Hershey
- University of Pittsburgh Medical Center, Pittsburgh
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 31 jan. 2025 · NCT04174157Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.