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Majaribio ya kliniki ya Magonjwa ya Kurithi katika jimbo la New York

Masomo 7 ya Magonjwa ya Kurithi yanatafuta washiriki katika vituo vya jimbo la New York.

Miji katika jimbo la New York

Maandishi rasmi ya utafiti (Kiingereza)

Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)

  • Icahn School of Medicine at Mount Sinai, New York
InaajiriUtafiti wa uchunguzi
7 Months – 15 Months · Jinsia zote · Imesasishwa 31 Ago 2026 · NCT06805695

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • Jacobi Medical Center, The Bronx
InaajiriHatua 2
Umri 18 na zaidi · Jinsia zote · Imesasishwa 5 Ago 2026 · NCT07224360

Helix Research Network

  • Rochester Regional Health (GenoWell), Rochester
InaajiriUtafiti wa uchunguziWajitolea wenye afya wanakaribishwa
Umri 18 na zaidi · Jinsia zote · Imesasishwa 23 Mac 2026 · NCT06057181

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Icahn School of Medicine at Mount Sinai, New York
InaajiriHatua 1/2
Umri 1 na zaidi · Jinsia zote · Imesasishwa 23 Mac 2026 · NCT05130437

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • New York Presbyterian Hospital - Morgan Stanley Children's Hospital, New York
InaajiriHatua 3
Umri 12 hadi 35 · Jinsia zote · Imesasishwa 23 Mac 2026 · NCT05477563

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Icahn School of Medicine at Mount Sinai - Clinical Research Unit, New York
InaajiriHatua 1/2
Umri wote · Jinsia zote · Imesasishwa 22 Jan 2026 · NCT04159103

STXBP1 and SYNGAP1 Related Disorders Natural History Study

  • Weill Cornell Medicine, New York
InaajiriUtafiti wa uchunguzi
Umri wote · Jinsia zote · Imesasishwa 29 Okt 2025 · NCT06555965

Kutoka ClinicalTrials.gov, data iliyopatikana 5 Okt 2026. Kila utafiti una masharti yake ya kufaa; timu ya utafiti huamua nani anaweza kujiunga.