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Nyumbani › Phenylketonuria

Majaribio ya kliniki ya Phenylketonuria yanayovutia washiriki nchini Marekani

Masomo 14 ya Phenylketonuria yanavutia washiriki katika vituo vya Marekani nzima.

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Maandishi rasmi ya utafiti (Kiingereza)

A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria

InaajiriHatua 1
Umri 18 hadi 69 · Jinsia zote · Imesasishwa 28 Sep 2026 · NCT07241234

A Study of Sepiapterin in Participants With Phenylketonuria (PKU)

InaajiriHatua 3
Hadi umri 9 · Jinsia zote · Imesasishwa 28 Ago 2026 · NCT06302348

PheCheck™ Validation Study

InaajiriUtafiti wa uchunguzi
Umri 1 na zaidi · Jinsia zote · Imesasishwa 25 Ago 2026 · NCT07551921

A Study of MZE782 in Adults With PKU

InaajiriHatua 2
Umri 18 hadi 75 · Jinsia zote · Imesasishwa 20 Ago 2026 · NCT07694440

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

InaajiriHatua 1/2
Umri 18 hadi 55 · Jinsia zote · Imesasishwa 18 Ago 2026 · NCT06332807

A Trial to Examine if Repinatrabit is Processed Differently in Adults With Reduced Liver or Kidney Function Compared to Adults With Normal Liver and Kidney Function

InaajiriHatua 1Wajitolea wenye afya wanakaribishwa
Umri 18 hadi 65 · Jinsia zote · Imesasishwa 12 Ago 2026 · NCT07713758

A Study of JNT-517 in Participants With Phenylketonuria (PKU)

InaajiriHatua 3
Umri 18 na zaidi · Jinsia zote · Imesasishwa 8 Jul 2026 · NCT06971731

Immune Modulation During Palynziq® Treatment in Adults (IMPALA)

InaajiriHatua 4
Umri 18 hadi 65 · Jinsia zote · Imesasishwa 17 Jun 2026 · NCT07477691

A Long-Term Study of JNT-517 in Participants With Phenylketonuria

InaajiriHatua 3
Umri 4 na zaidi · Jinsia zote · Imesasishwa 1 Mei 2026 · NCT06628128

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

InaajiriUtafiti wa uchunguzi
Umri wote · Jinsia zote · Imesasishwa 25 Mac 2026 · NCT05813678

A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)

InaajiriUtafiti wa uchunguzi
Umri wote · Jinsia zote · Imesasishwa 24 Mac 2026 · NCT06305234

Nutritional Impacts of Palynziq on Patients With Phenylketonuria (PKU)

InaajiriUtafiti wa uchunguzi
Umri 16 na zaidi · Jinsia zote · Imesasishwa 14 Jan 2026 · NCT04404530

Development of Novel Psychological Assessment Tools and Anxiety Intervention for Phenylketonuria

Inaajiri
Umri 10 hadi 17 · Jinsia zote · Imesasishwa 23 Des 2025 · NCT06560736

Kutoka ClinicalTrials.gov, data iliyopatikana 5 Okt 2026. Kila utafiti una masharti yake ya kufaa; timu ya utafiti huamua nani anaweza kujiunga.