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Majaribio ya kliniki ya Atrofi ya Misuli ya Utani katika jimbo la Illinois
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A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Ann and Robert H. Lurie Children Hospital of Chicago, Chicago
InaajiriHatua 4
3 Months – 24 Months · Jinsia zote · Imesasishwa 2 Okt 2026 · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
InaajiriHatua 2
Umri 5 hadi 17 · Jinsia zote · Imesasishwa 14 Sep 2026 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
InaajiriHatua 1
Umri 3 na zaidi · Jinsia zote · Imesasishwa 3 Sep 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Lurie Childrens Hospital, Chicago
Inaajiri
Umri 3 na zaidi · Jinsia zote · Imesasishwa 19 Ago 2026 · NCT05866419A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
- Ann and Robert H Lurie Childrens Hospital of Chicago, Chicago
InaajiriHatua 3
0 Days – 42 Days · Jinsia zote · Imesasishwa 18 Ago 2026 · NCT07221669ALS/MND Natural History Study Data Repository
- Northwestern University, Chicago
InaajiriUtafiti wa uchunguzi
Umri 18 hadi 90 · Jinsia zote · Imesasishwa 20 Mei 2026 · NCT05966038Kutoka ClinicalTrials.gov, data iliyopatikana 5 Okt 2026. Kila utafiti una masharti yake ya kufaa; timu ya utafiti huamua nani anaweza kujiunga.