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Duchenne Muscular Dystrophy clinical trials in Missouri
3 studies for Duchenne Muscular Dystrophy are looking for participants at sites in Missouri.
Cities in Missouri
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
- Washington University in St. Louis, St Louis
RecruitingPhase 1
Ages 2 and older · Men · Updated Sep 11, 2026 · NCT04626674A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
- Washington University in St. Louis, St Louis
RecruitingPhase 1/2
Ages 0 to 17 · Men · Updated Jul 8, 2026 · NCT06138639PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)
- Washington University School of Medicine, St Louis
RecruitingPhase 1/2
Ages 2 to 7 · Men · Updated Jun 23, 2026 · NCT07429240From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.