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Fabry Disease clinical trials in Pennsylvania
5 studies for Fabry Disease are looking for participants at sites in Pennsylvania.
Cities in Pennsylvania
Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingPhase 1/2
Ages 18 to 65 · Men · Updated Sep 24, 2026 · NCT06270316A Study of Patients With Fabry Disease (US Specific)
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingObservational study
Ages 18 and older · All sexes · Updated Sep 9, 2026 · NCT06906367A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecruitingPhase 3
Ages 2 to 11 · All sexes · Updated Sep 1, 2026 · NCT06904261Fabry Disease Registry & Pregnancy Sub-registry
- Geisinger Medical Center- Site Number : 840111, Danville
- Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- and 2 more
RecruitingObservational study
All ages · All sexes · Updated Jun 23, 2026 · NCT00196742A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding
- Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
RecruitingObservational study
All ages · Women · Updated Jul 8, 2025 · NCT04252066From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.