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Transthyretin-Related Hereditary Amyloidosis clinical trials in California
5 studies for Transthyretin-Related Hereditary Amyloidosis are looking for participants at sites in California.
Cities in California
Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis
- Research Site, La Jolla
- Research Site, Los Angeles
- Research Site, San Francisco
- and 1 more
RecruitingObservational study
Ages 18 to 130 · All sexes · Updated Sep 23, 2026 · NCT06465810Long-term Safety of Eplontersen Treated aTTR Patients and in Liver Transplant and Severely Hepatic Impaired Subpopulations
- Research Site, Los Angeles
RecruitingObservational study
Ages 18 and older · All sexes · Updated Sep 14, 2026 · NCT07654855ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)
- Clinical Trial Site, La Jolla
- Clinical Trial Site, Los Angeles
RecruitingObservational study
All ages · All sexes · Updated Sep 8, 2026 · NCT04561518Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant
- University of California, San Diego (UCSD) - Medical Center, La Jolla
- University of California, Los Angeles (UCLA) - David Geffen School of Medicine, Los Angeles
- University of California, San Francisco (UCSF), San Francisco
- and 1 more
RecruitingPhase 3
Ages 18 to 75 · All sexes · Updated Aug 4, 2026 · NCT06563895MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)
- Cedars-Sinai Medical Center, Los Angeles
- Western Greater Los Angeles VA Medical Center, Los Angeles
- Stanford University, Palo Alto
- and 1 more
RecruitingPhase 3
Ages 18 to 90 · All sexes · Updated Mar 27, 2026 · NCT06128629From ClinicalTrials.gov, data retrieved Oct 6, 2026. Each study sets its own eligibility; the study team decides who can join.