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በፍሎሪዳ ለየጋዜማ ገመድ ጡንቻ መኮማተር የሚደረጉ ክሊኒካዊ ጥናቶች

ለየጋዜማ ገመድ ጡንቻ መኮማተር የሚደረጉ 8 ጥናቶች በፍሎሪዳ ባሉ ቦታዎች ተሳታፊዎችን እየፈለጉ ነው።

በፍሎሪዳ ውስጥ ያሉ ከተሞች

Official study text (English)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • University of Florida Pediatrics, Gainesville
ተሳታዮችን በመፈለግ ላይደረጃ 4
3 Months – 24 Months · ሁሉም ጾታዎች · የተሻሻለው በ2 ኦክቶ 2026 · NCT05861986

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Rare Disease Research FL LLC, Kissimmee
ተሳታዮችን በመፈለግ ላይደረጃ 2
እድሜ ከ5 እስከ 17 · ሁሉም ጾታዎች · የተሻሻለው በ14 ሴፕቴ 2026 · NCT07287982

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • University of Florida Pediatrics, Gainesville
ተሳታዮችን በመፈለግ ላይደረጃ 4
3 Months – 24 Months · ሁሉም ጾታዎች · የተሻሻለው በ10 ሴፕቴ 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Nemours Children's Hospital, Orlando, Orlando
ተሳታዮችን በመፈለግ ላይደረጃ 1
እድሜ 3 እና ከዚያ በላይ · ሁሉም ጾታዎች · የተሻሻለው በ3 ሴፕቴ 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Nemours Children's Hospital, Florida, Orlando
ተሳታዮችን በመፈለግ ላይ
እድሜ 3 እና ከዚያ በላይ · ሁሉም ጾታዎች · የተሻሻለው በ19 ኦገስ 2026 · NCT05866419

Clinical Procedures to Support Research in ALS

  • University of Miami, Miami
ተሳታዮችን በመፈለግ ላይየመመልከት ጥናት
እድሜ 18 እና ከዚያ በላይ · ሁሉም ጾታዎች · የተሻሻለው በ15 ጁን 2026 · NCT03489278

ALS/MND Natural History Study Data Repository

  • University of Florida, Gainesville
ተሳታዮችን በመፈለግ ላይየመመልከት ጥናት
እድሜ ከ18 እስከ 90 · ሁሉም ጾታዎች · የተሻሻለው በ20 ሜይ 2026 · NCT05966038

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Golisano Children's Hospital of Southwest Florida, Fort Myers
  • Jackson South Medical Center, Palmetto Bay
ተሳታዮችን በመፈለግ ላይየመመልከት ጥናት
ለሁሉም እድሜ · ሁሉም ጾታዎች · የተሻሻለው በ31 ጃንዩ 2025 · NCT04174157

ከ ClinicalTrials.gov የተገኘ መረጃ፣ በ5 ኦክቶ 2026 የተሰብሰቡ። እያንዳንዱ ጥናት የራሱን ቅድመ ሁኔታ ይወስናል፤ የጥናት ቡድኑ ማን መሳተፍ እንደሚችል ይወስናል።