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Alpha-1 Antitrypsin Deficiency clinical trials in California

4 studies for Alpha-1 Antitrypsin Deficiency are looking for participants at sites in California.

Cities in California

Study to Check the Safety of Fazirsiran and Learn if Fazirsiran Can Help People With Liver Disease and Scarring (Fibrosis) Due to an Abnormal Version of Alpha-1 Antitrypsin Protein

  • University of California San Diego, Altman Clinical and Translational Institute, La Jolla
  • UCLA Pulmonary and Critical Care, Los Angeles
  • Stanford University, Palo Alto
  • and 1 more
RecruitingPhase 3
Ages 18 to 75 · All sexes · Updated May 13, 2026 · NCT05677971

Study to Learn About the Safety of Fazirsiran and if it Can Help People With Alpha-1 Antitrypsin Liver Disease With Mild Liver Scarring (Fibrosis)

  • University of California San Diego, La Jolla
  • UCLA Pulmonary and Critical Care, Los Angeles
  • University of California Benioff Children's Hospital, San Francisco
RecruitingPhase 3
Ages 18 to 75 · All sexes · Updated Mar 5, 2026 · NCT06165341

PiMZ Longitudinal Cohort (PiMZ Logic)

  • University of California- Los Angeles, Los Angeles
RecruitingObservational study
Ages 18 and older · All sexes · Updated Jan 16, 2026 · NCT06505603

From ClinicalTrials.gov, data retrieved Oct 1, 2026. Each study sets its own eligibility; the study team decides who can join.