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Aplastic Anemia clinical trials recruiting in the U.S.
26 studies for Aplastic Anemia are recruiting participants at sites across the United States.
Aplastic anemia is a rare but serious blood disorder. If you have it, your bone marrow doesn't make enough new blood cells. Read more on the causes.
Cities with the most studies
- Washington, DC8 studies
- Baldwin Park, CA5 studies
- Atlanta, GA4 studies
- Durham, NC4 studies
- Nashville, TN4 studies
- Philadelphia, PA4 studies
- Milwaukee, WI4 studies
- St. Louis, MO4 studies
- New York City, NY4 studies
- Baltimore, MD3 studies
- Seattle, WA3 studies
- Columbus, OH3 studies
- Birmingham, AL3 studies
- Detroit, MI3 studies
- Houston, TX3 studies
- Richmond, VA3 studies
- Memphis, TN3 studies
By state
- Alabama3 studies
- California5 studies
- Florida4 studies
- Georgia4 studies
- Maryland10 studies
- Michigan3 studies
- Minnesota3 studies
- Missouri4 studies
- New York6 studies
- North Carolina4 studies
- Ohio4 studies
- Pennsylvania5 studies
- Tennessee6 studies
- Texas3 studies
- Virginia3 studies
- Washington3 studies
- Wisconsin4 studies
Recently updated studies
Pacritinib, a Kinase Inhibitor of CSF1R, IRAK1, JAK2, and FLT3, in Adults and Pediatric Participants 12 Years of Age or Older With Myelodysplastic Syndromes or Myelodysplastic/Myeloproliferative Neoplasms
RecruitingPhase 1/2
Ages 12 to 120 · All sexes · Updated Oct 1, 2026 · NCT06303193Unrelated Umbilical Cord Blood Transplantation for Severe Aplastic Anemia and Hypo-plastic MDS Using CordIn(TM), Umbilical Cord Blood-Derived Ex Vivo Expanded Stem and Progenitor Cells to Expedite Engraftment and Improve Transplant Outcome
RecruitingPhase 1/2
Ages 4 to 75 · All sexes · Updated Oct 1, 2026 · NCT03173937Cancer in Inherited Bone Marrow Failure Syndromes
RecruitingObservational studyHealthy volunteers welcome
1 Day – 100 Years · All sexes · Updated Sep 30, 2026 · NCT00027274Natural History of Acquired and Inherited Bone Marrow Failure Syndromes
RecruitingObservational study
Ages 2 to 99 · All sexes · Updated Sep 30, 2026 · NCT05012111Darzalex Faspro (Daratumumab and Hyaluronidase-fihj) Before Standard Desensitization and Allogeneic Peripheral Blood Stem Cell Transplantation in Adult Patients at High-risk for Primary Graft Failure Secondary to Donor Specific Antibodies
RecruitingEarly phase 1
Ages 18 and older · All sexes · Updated Sep 24, 2026 · NCT06398457Allogeneic Hematopoietic Stem Cell Transplantation for Severe Aplastic Anemia and Other Bone Marrow Failure Syndromes Using G-CSF Mobilized CD34+ Selected Hematopoietic Precursor Cells Co-Infused With a Reduced Dose of Non-Mobilized Donor T-cells
RecruitingPhase 2
Ages 4 to 80 · All sexes · Updated Sep 22, 2026 · NCT01174108Haploidentical HCT for Severe Aplastic Anemia
RecruitingPhase 2
Up to age 21 · All sexes · Updated Sep 16, 2026 · NCT04558736Haplo-identical Transplantation for Severe Aplastic Anemia, Hypo-plastic MDS and PNH Using Peripheral Blood Stem Cells and Post-transplant Cyclophosphamide for GVHD Prophylaxis
RecruitingPhase 2
Ages 4 to 75 · All sexes · Updated Sep 8, 2026 · NCT03520647The HOPE Biobank Resource (BMT CTN 2402 HOPE)
RecruitingObservational studyHealthy volunteers welcome
All ages · All sexes · Updated Aug 27, 2026 · NCT07227155A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
RecruitingObservational study
All ages · All sexes · Updated Jul 6, 2026 · NCT01351545TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Non-Malignant Hematological Disorders in Children
RecruitingPhase 2
Ages 0 to 21 · All sexes · Updated Jul 1, 2026 · NCT04356469Methylprednisolone, Horse Anti-Thymocyte Globulin, Cyclosporine, Filgrastim, and/or Pegfilgrastim or Pegfilgrastim Biosimilar in Treating Patients With Aplastic Anemia or Low or Intermediate-Risk Myelodysplastic Syndrome
RecruitingPhase 2
Ages 18 and older · All sexes · Updated Jun 22, 2026 · NCT01624805Let's Get REAL: Family Health Communication Tool in Pediatric Stem Cell Transplant and Cellular Therapy
Recruiting
Ages 8 and older · All sexes · Updated Jun 4, 2026 · NCT06689800MT2023-20: Hematopoietic Cell Transplant With Reduced Intensity Conditioning and Post-transplant Cyclophosphamide for Severe Aplastic Anemia and Other Forms of Acquired Bone Marrow Failure.
RecruitingPhase 2
Ages 0 to 75 · All sexes · Updated Jun 3, 2026 · NCT06412497Haploidentical Bone Marrow Transplant With Post-Transplant Cyclophosphamide for Patients With Severe Aplastic Anemia
RecruitingPhase 2
Ages 1 to 75 · All sexes · Updated Apr 20, 2026 · NCT02828592Early Initiation of Oral Therapy With Cyclosporine and Eltrombopag for Treatment Naive Severe Aplastic Anemia (SAA)
RecruitingPhase 2
Ages 3 to 99 · All sexes · Updated Mar 9, 2026 · NCT04304820Clinical Trial of Upfront Haploidentical or Unrelated Donor BMT to Restore Normal Hematopoiesis in Aplastic Anemia
RecruitingPhase 2
Ages 3 to 75 · All sexes · Updated Feb 17, 2026 · NCT06517641Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders
RecruitingPhase 2
Up to age 65 · All sexes · Updated Jan 30, 2026 · NCT03579875A Reduced-Intensity Conditioning Regimen (Cyclophosphamide, Pentostatin, Anti-thymocyte Globulin) Followed by Haploidentical Hematopoietic Stem Cell Transplant for the Treatment of Patients With Refractory or Recurrent Severe Aplastic Anemia
RecruitingPhase 1Healthy volunteers welcome
Up to age 75 · All sexes · Updated Jan 5, 2026 · NCT05757310A Study of Emapalumab for Pediatric Aplastic Anemia
RecruitingPhase 2Healthy volunteers welcome
Ages 0 to 25 · All sexes · Updated Dec 17, 2025 · NCT06430788Exercise Training and NR Supplementation Trial to Improve Fitness in AYA HCT Survivors
RecruitingPhase 2
Ages 10 to 30 · All sexes · Updated Dec 4, 2025 · NCT05194397Two Step Haplo With Radiation Conditioning
RecruitingPhase 2
Ages 18 and older · All sexes · Updated Oct 30, 2025 · NCT05031897Tissue, Blood, and Body Fluid Sample Collection From Patients With Hematologic Cancer
RecruitingObservational study
Ages 18 to 120 · All sexes · Updated Oct 27, 2025 · NCT01137643Umbilical Cord Blood Transplantation From Unrelated Donors
RecruitingObservational study
2 Months – 75 Years · All sexes · Updated Oct 10, 2025 · NCT03016806HPC Offered for PRESERVE Expansion
RecruitingObservational study
Ages 12 to 80 · All sexes · Updated Aug 28, 2025 · NCT07145411From ClinicalTrials.gov, data retrieved Oct 2, 2026. Each study sets its own eligibility; the study team decides who can join.