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Familial Amyloidosis clinical trials recruiting in the U.S.
5 studies for Familial Amyloidosis are recruiting participants at sites across the United States.
Cities with the most studies
- New York City, NY4 studies
- Houston, TX3 studies
- Baltimore, MD3 studies
- Los Angeles, CA3 studies
- San Diego, CA3 studies
- Durham, NC3 studies
- Philadelphia, PA3 studies
- Dallas, TX3 studies
By state
- California3 studies
- Maryland3 studies
- New York4 studies
- North Carolina3 studies
- Ohio3 studies
- Pennsylvania3 studies
- Texas4 studies
Recently updated studies
Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis
RecruitingObservational study
Ages 18 to 130 · All sexes · Updated Sep 23, 2026 · NCT06465810ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)
RecruitingObservational study
All ages · All sexes · Updated Sep 8, 2026 · NCT04561518Patisiran-Lipid Nanoparticle (LNP) Pregnancy Surveillance Program
RecruitingObservational study
All ages · Women · Updated Sep 8, 2026 · NCT05040373Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR Carriers
RecruitingObservational study
Ages 30 to 80 · All sexes · Updated Aug 31, 2026 · NCT05489549MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)
RecruitingPhase 3
Ages 18 to 90 · All sexes · Updated Mar 27, 2026 · NCT06128629From ClinicalTrials.gov, data retrieved Oct 1, 2026. Each study sets its own eligibility; the study team decides who can join.