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Familial Amyloidosis clinical trials in Pennsylvania
3 studies for Familial Amyloidosis are looking for participants at sites in Pennsylvania.
Cities in Pennsylvania
MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)
- Penn Presbyterian Medical Center, Philadelphia
- Allegheny General Hospital, Pittsburgh
- University of Pittsburgh Medical Center, Pittsburgh
RecruitingPhase 3
Ages 18 to 90 · All sexes · Updated Nov 4, 2026 · NCT06128629ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)
- Clinical Trial Site, Philadelphia
RecruitingObservational study
All ages · All sexes · Updated Oct 13, 2026 · NCT04561518Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis
- Research Site, Danville
- Research Site, Philadelphia
- Research Site, Philadelphia
RecruitingObservational study
Ages 18 to 130 · All sexes · Updated Sep 23, 2026 · NCT06465810From ClinicalTrials.gov, data retrieved Nov 15, 2026. Each study sets its own eligibility; the study team decides who can join.