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Genetic Disorders clinical trials in Miami, FL
5 studies for Genetic Disorders are looking for participants at sites in and around Miami (within about 30 miles). Open a study to see who can join and how to contact the study team.
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
RecruitingObservational studyHealthy volunteers welcome
- University of Miami Miller School of Medicine, Miami
A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
RecruitingPhase 3
- GC2501 Study Site 105, Miami
Rett Syndrome Registry
RecruitingObservational study
- Nicklaus Children's Hospital, Miami
A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)
RecruitingObservational study
- Sirven and Associates, Miami
Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
RecruitingPhase 1/2
- Nicklaus Children's Hospital, Miami
About Genetic Disorders
A mutation in a person's genes can cause a medical condition called a genetic disorder. Learn about the types and how they are detected.
More about Genetic Disorders on MedlinePlus
Genetic Disorders trials in other cities
- Washington, DC12 studies
- Philadelphia, PA9 studies
- Houston, TX8 studies
- Los Angeles, CA7 studies
- Durham, NC7 studies
- Mountain View, CA6 studies
- New York City, NY6 studies
- Boston, MA6 studies
- Aurora, CO5 studies
- Chicago, IL5 studies
- San Diego, CA5 studies
- Dallas, TX4 studies
Other studies in Miami
- Breast Cancer42 studies
- Cancer (all types)36 studies
- Non-Small Cell Lung Cancer31 studies
- Prostate Cancer28 studies
- Obesity27 studies
- Acute Myeloid Leukemia24 studies
- Overweight23 studies
- Ovarian Cancer23 studies
- Metastatic Cancer23 studies
- Ulcerative Colitis22 studies
- Alzheimer's Disease21 studies
- Multiple Myeloma21 studies
From ClinicalTrials.gov, data retrieved Sep 29, 2026. Each study sets its own eligibility; the study team decides who can join.