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Genetic Disorders clinical trials in Ohio
7 studies for Genetic Disorders are looking for participants at sites in Ohio.
Cities in Ohio
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
- Cincinnati Children's Hospital Medical Center, Cincinnati
RecruitingPhase 2/3
Ages 2 to 17 · All sexes · Updated Sep 24, 2026 · NCT07441876Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Ohio State University - Neurology, Columbus
RecruitingObservational studyHealthy volunteers welcome
All ages · All sexes · Updated Sep 1, 2026 · NCT06016946A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
- GC2501 Study Site 104, Cleveland
RecruitingPhase 3
Ages 18 to 80 · All sexes · Updated Aug 11, 2026 · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- Ohio State University, Columbus
RecruitingPhase 2
Ages 18 and older · All sexes · Updated Aug 5, 2026 · NCT07224360Prospective Clinical Assessment Study in Children With Hypochondroplasia
- Cincinnati Children's Hospital Medical Center, Cincinnati
RecruitingObservational study
30 Months – 16 Years · All sexes · Updated Jul 16, 2026 · NCT06410976Rett Syndrome Registry
- Cincinnati Children's Hospital Medical Center, Cincinnati
- Nationwide Children's Hospital, Columbus
RecruitingObservational study
Ages 0 to 99 · All sexes · Updated Jun 30, 2026 · NCT05432349Helix Research Network
- TriHealth (DNA Discovery), Cincinnati
- The Ohio State University (Genomic Health), Columbus
RecruitingObservational studyHealthy volunteers welcome
Ages 18 and older · All sexes · Updated Mar 23, 2026 · NCT06057181From ClinicalTrials.gov, data retrieved Oct 3, 2026. Each study sets its own eligibility; the study team decides who can join.