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Myotonic Dystrophy clinical trials in Pennsylvania
3 studies for Myotonic Dystrophy are looking for participants at sites in Pennsylvania.
A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- Penn Medicine: University of Pennsylvania Health System- Site Number : 8400009, Philadelphia
RecruitingPhase 1/2
Ages 10 to 55 · All sexes · Updated Sep 21, 2026 · NCT06844214Biomarker Development for Muscular Dystrophies
- University of Pittsburgh, Pittsburgh
RecruitingObservational studyHealthy volunteers welcome
Ages 5 and older · All sexes · Updated Nov 24, 2025 · NCT05019625Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
- University of Pittsburgh Medical Center, Pittsburgh
RecruitingPhase 2/3
Ages 6 to 45 · All sexes · Updated May 28, 2025 · NCT05004129From ClinicalTrials.gov, data retrieved Sep 30, 2026. Each study sets its own eligibility; the study team decides who can join.