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Rare Diseases clinical trials in Tennessee
5 studies for Rare Diseases are looking for participants at sites in Tennessee.
Cities in Tennessee
A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia
- Vanderbilt University Medical Center, Nashville
RecruitingPhase 1/2
Ages 18 to 65 · All sexes · Updated Sep 21, 2026 · NCT06525636Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- Vanderbilt University Medical Center, Nashville
RecruitingObservational studyHealthy volunteers welcome
1 Month – 100 Years · All sexes · Updated Sep 18, 2026 · NCT02450851Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- St. Jude Children's Research Hospital, Memphis
RecruitingObservational studyHealthy volunteers welcome
All ages · All sexes · Updated Sep 1, 2026 · NCT06016946Stakeholders of Rare Diseases Informing Values In Neuroethics
- St. Jude Children's Research Hospital, Memphis
RecruitingObservational study
All ages · All sexes · Updated Jul 13, 2026 · NCT07314736The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
- Vanderbilt University, Nashville
RecruitingPhase 2
Ages 12 and older · All sexes · Updated Jul 1, 2025 · NCT04372615From ClinicalTrials.gov, data retrieved Sep 30, 2026. Each study sets its own eligibility; the study team decides who can join.