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Spinal Muscular Atrophy clinical trials in Gainesville, FL
3 studies for Spinal Muscular Atrophy are looking for participants at sites in and around Gainesville (within about 30 miles). Open a study to see who can join and how to contact the study team.
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
RecruitingPhase 4
- University of Florida Pediatrics, Gainesville
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
RecruitingPhase 4
- University of Florida Pediatrics, Gainesville
ALS/MND Natural History Study Data Repository
RecruitingObservational study
- University of Florida, Gainesville
About Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) attacks nerve cells in the spinal cord, weakening voluntary muscles. Read about the genetics, types, and what may help.
More about Spinal Muscular Atrophy on MedlinePlus
Spinal Muscular Atrophy trials in other cities
- New York City, NY9 studies
- Mountain View, CA8 studies
- Philadelphia, PA7 studies
- Norfolk, VA6 studies
- Chicago, IL6 studies
- Grand Rapids, MI6 studies
- Boston, MA5 studies
- Houston, TX5 studies
- Memphis, TN4 studies
- Phoenix, AZ4 studies
- Little Rock, AR4 studies
- Aurora, CO4 studies
Other studies in Gainesville
- Heart Failure13 studies
- Parkinson's Disease13 studies
- Type 1 Diabetes12 studies
- Breast Cancer12 studies
- Non-Small Cell Lung Cancer10 studies
- Colorectal Cancer9 studies
- Cardiovascular Disease9 studies
- Cancer (all types)9 studies
- Lung Cancer9 studies
- Prostate Cancer8 studies
- Mild Cognitive Impairment8 studies
- Acute Myeloid Leukemia8 studies
From ClinicalTrials.gov, data retrieved Oct 1, 2026. Each study sets its own eligibility; the study team decides who can join.