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Spinal Muscular Atrophy clinical trials in Missouri
3 studies for Spinal Muscular Atrophy are looking for participants at sites in Missouri.
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- The Curators of the University of Missouri on behalf of University of Missouri Health Care, Columbia
RecruitingPhase 2
Ages 5 to 17 · All sexes · Updated Oct 8, 2026 · NCT07287982ALS/MND Natural History Study Data Repository
- Saint Louis University, St Louis
RecruitingObservational study
Ages 18 to 90 · All sexes · Updated May 20, 2026 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- University of Missouri Health System, Columbia
- Washington University School of Medicine in St. Louis, St Louis
RecruitingObservational study
All ages · All sexes · Updated Jan 31, 2025 · NCT04174157From ClinicalTrials.gov, data retrieved Nov 15, 2026. Each study sets its own eligibility; the study team decides who can join.