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Leukoencefalopati kliniske forsøg i Pennsylvania

4 studier for Leukoencefalopati søger deltagere på steder i Pennsylvania.

Byer i Pennsylvania

Officiel studietekst (engelsk)

An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease

  • Children's Hospital of Philadelphia, Philadelphia
RekruttererFase 1/2
6 Months · Alle køn · Opdateret 24. sep. 2026 · NCT05757141

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 9. feb. 2026 · NCT03333200

North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)

  • The Children's Hospital of Philadelphia, Philadelphia
  • Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudieFrivillige med god helbredstilstand velkomne
Alle aldre · Alle køn · Opdateret 4. feb. 2026 · NCT01694940

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 23. okt. 2025 · NCT03047369

Fra ClinicalTrials.gov, data hentet 3. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.