Hjem › Leukoencefalopati › Pennsylvania
Leukoencefalopati kliniske forsøg i Pennsylvania
4 studier for Leukoencefalopati søger deltagere på steder i Pennsylvania.
Byer i Pennsylvania
Officiel studietekst (engelsk)
An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease
- Children's Hospital of Philadelphia, Philadelphia
RekruttererFase 1/2
6 Months · Alle køn · Opdateret 24. sep. 2026 · NCT05757141Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 9. feb. 2026 · NCT03333200North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
- The Children's Hospital of Philadelphia, Philadelphia
- Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservationsstudieFrivillige med god helbredstilstand velkomne
Alle aldre · Alle køn · Opdateret 4. feb. 2026 · NCT01694940The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 23. okt. 2025 · NCT03047369Fra ClinicalTrials.gov, data hentet 3. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.