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North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)

RecruitingObservational studyHealthy volunteers welcome

Who can join

All ages · All sexes · Healthy volunteers welcome

Full eligibility criteria
Inclusion Criteria:

* Patients diagnosed with or suspected to have a mitochondrial disorder
* Adult carriers of known mitochondrial DNA mutations
* Patients with laboratory analysis indicative of a mitochondrial disorder.
* Medical information and tissue samples are also accepted from deceased individuals who fulfill the above criteria.

Exclusion Criteria:

* Patients not suspected of having a mitochondrial disorder
* Patients not suspected of carrying a mitochondrial DNA or nuclear DNA mutation that affects mitochondrial function.

About the study

The North American Mitochondrial Disease Consortium (NAMDC) maintains a patient contact registry and tissue biorepository for patients with mitochondrial disorders.

Sponsor: Columbia University · Participants: 1,000 · Started: Jan 31, 2011

Contact the study team

Official record on ClinicalTrials.gov — NCT01694940

Locations in the U.S.

CaliforniaUniversity of California San Diego, San Diego
Lucile Packard Children's Hospital, Stanford
ColoradoChildren's Hospital of Colorado, Aurora
District of ColumbiaChildren's National Medical Center, Washington D.C.
FloridaUniversity of Florida, Gainsville
MassachusettsMassachusetts General Hospital, Boston
MinnesotaMayo Clinic, Rochester
New YorkColumbia University Medical Center, New York
Virtual Site (Remote enrollment), New York
OhioAkron Children's Hospital, Akron
Cleveland Clinic, Cleveland
Case Western Reserve University, Clevland
PennsylvaniaThe Children's Hospital of Philadelphia, Philadelphia
Children's Hospital of Pittsburgh, Pittsburgh
TexasBaylor College of Medicine, Houston
WashingtonSeattle Children's Hospital and Regional Medical Center, Seattle

Conditions

From ClinicalTrials.gov, data retrieved Sep 30, 2026. Each study sets its own eligibility; the study team decides who can join.