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Myotonisk dystrofi kliniske forsøg i Virginia
8 studier for Myotonisk dystrofi søger deltagere på steder i Virginia.
Byer i Virginia
Officiel studietekst (engelsk)
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- Virginia Commonwealth University - Biotech One, Richmond
RekruttererFase 3
Alder 16 og opefter · Alle køn · Opdateret 1. okt. 2026 · NCT07486934A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- Virginia Commonwealth University Medical Center- Site Number : 8400006, Richmond
RekruttererFase 1/2
Alder 10 til 55 · Alle køn · Opdateret 21. sep. 2026 · NCT06844214Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
- Virginia Commonwealth University, Richmond
RekruttererObservationsstudie
Alder 18 til 70 · Alle køn · Opdateret 4. sep. 2026 · NCT07700225Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
- Virginia Commonwealth University, Richmond
RekruttererObservationsstudie
Alder 3 til 17 · Alle køn · Opdateret 11. aug. 2026 · NCT06747884DMCRN-02-001: Assessing Pediatric Endpoints in DM1
- Virginia Commonwealth University, Richmond
RekruttererObservationsstudie
59 Months · Alle køn · Opdateret 10. jun. 2026 · NCT05224778Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- Virginia Commonwealth University, Richmond
RekruttererObservationsstudie
Alder 18 til 70 · Alle køn · Opdateret 10. jun. 2026 · NCT03981575Study of ATX-01 in Participants With DM1
- Virginia Commonwealth University, Richmond
RekruttererFase 1/2
Alder 18 til 64 · Alle køn · Opdateret 10. feb. 2026 · NCT06300307Long-Term Development of Muscular Dystrophy Outcome Assessments
- Virginia Commonwealth University, Richmond
RekruttererObservationsstudie
Alder 6 til 50 · Alle køn · Opdateret 18. nov. 2025 · NCT05989620Fra ClinicalTrials.gov, data hentet 4. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.