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Myotonisk dystrofi kliniske forsøg i Richmond, VA
8 studier for Myotonisk dystrofi søger deltagere på steder i og omkring Richmond (inden for ca. 30 miles). Åbn et studie for at se, hvem der kan deltage, og hvordan man kontakter studieteamet.
Officiel studietekst (engelsk)
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Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
RekruttererFase 3
- Virginia Commonwealth University - Biotech One, Richmond
A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
RekruttererFase 1/2
- Virginia Commonwealth University Medical Center- Site Number : 8400006, Richmond
Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
RekruttererObservationsstudie
- Virginia Commonwealth University, Richmond
Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
RekruttererObservationsstudie
- Virginia Commonwealth University, Richmond
DMCRN-02-001: Assessing Pediatric Endpoints in DM1
RekruttererObservationsstudie
- Virginia Commonwealth University, Richmond
Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
RekruttererObservationsstudie
- Virginia Commonwealth University, Richmond
Study of ATX-01 in Participants With DM1
RekruttererFase 1/2
- Virginia Commonwealth University, Richmond
Long-Term Development of Muscular Dystrophy Outcome Assessments
RekruttererObservationsstudie
- Virginia Commonwealth University, Richmond
Myotonisk dystrofi forsøg i andre byer
- Rochester, NY7 studier
- Boston, MA4 studier
- Los Angeles, CA4 studier
- Cedar Rapids, IA3 studier
- Gainesville, FL3 studier
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Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.