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Fenylketonuri kliniske forsøg i Pennsylvania

8 studier for Fenylketonuri søger deltagere på steder i Pennsylvania.

Byer i Pennsylvania

Officiel studietekst (engelsk)

A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererFase 1
Alder 18 til 69 · Alle køn · Opdateret 28. sep. 2026 · NCT07241234

A Study of MZE782 in Adults With PKU

  • Clinic for Special Children, Gordonville
RekruttererFase 2
Alder 18 til 75 · Alle køn · Opdateret 20. aug. 2026 · NCT07694440

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

  • University of Pittsburgh Medical Center, Pittsburgh
RekruttererFase 1/2
Alder 18 til 55 · Alle køn · Opdateret 18. aug. 2026 · NCT06332807

A Study of JNT-517 in Participants With Phenylketonuria (PKU)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
RekruttererFase 3
Alder 18 og opefter · Alle køn · Opdateret 8. jul. 2026 · NCT06971731

Immune Modulation During Palynziq® Treatment in Adults (IMPALA)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Philadelphia
RekruttererFase 4
Alder 18 til 65 · Alle køn · Opdateret 17. jun. 2026 · NCT07477691

A Long-Term Study of JNT-517 in Participants With Phenylketonuria

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
RekruttererFase 3
Alder 4 og opefter · Alle køn · Opdateret 1. maj 2026 · NCT06628128

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

  • University of Pittsburgh Medical Center, Pittsburgh
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 25. mar. 2026 · NCT05813678

A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)

  • University of Pittsburgh Medical Center, Pittsburgh
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 24. mar. 2026 · NCT06305234

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.