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Phenylketonuria clinical trials in Pittsburgh, PA
6 studies for Phenylketonuria are looking for participants at sites in and around Pittsburgh (within about 30 miles). Open a study to see who can join and how to contact the study team.
Recruiting for a study here? Feature it at the top of this page — $99 for 30 days →
A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria
RecruitingPhase 1
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)
RecruitingPhase 1/2
- University of Pittsburgh Medical Center, Pittsburgh
A Study of JNT-517 in Participants With Phenylketonuria (PKU)
RecruitingPhase 3
- University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
A Long-Term Study of JNT-517 in Participants With Phenylketonuria
RecruitingPhase 3
- University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)
RecruitingObservational study
- University of Pittsburgh Medical Center, Pittsburgh
A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)
RecruitingObservational study
- University of Pittsburgh Medical Center, Pittsburgh
About Phenylketonuria
In phenylketonuria (PKU), your body can't process phenylalanine, an amino acid in most foods. Read about genetics, screening, and special diets.
More about Phenylketonuria on MedlinePlus
Phenylketonuria trials in other cities
- Dallas, TX7 studies
- Indianapolis, IN6 studies
- Chicago, IL5 studies
- Portland, OR5 studies
- Salt Lake City, UT4 studies
- Atlanta, GA4 studies
- Boston, MA3 studies
- Tampa, FL3 studies
- Nashville, TN3 studies
- Aurora, CO3 studies
- Milwaukee, WI3 studies
Other studies in Pittsburgh
- Non-Small Cell Lung Cancer48 studies
- Cancer (all types)41 studies
- Breast Cancer39 studies
- Colorectal Cancer32 studies
- Metastatic Cancer31 studies
- Melanoma31 studies
- Ovarian Cancer30 studies
- Endometrial Cancer23 studies
- Lung Cancer23 studies
- Prostate Cancer23 studies
- Stroke22 studies
- Head and Neck Squamous Cell Carcinoma22 studies
From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.