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Seglcelle-anæmi kliniske forsøg i Massachusetts
10 studier for Seglcelle-anæmi søger deltagere på steder i Massachusetts.
Byer i Massachusetts
Officiel studietekst (engelsk)
A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease
- Boston Children's Hospital, Boston
- Boston Medical Center, Boston
RekruttererFase 3
Alder 12 og opefter · Alle køn · Opdateret 17. sep. 2026 · NCT06612268A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease
- Boston Childrens Hospital, Boston
RekruttererFase 1/2Frivillige med god helbredstilstand velkomne
Alder 12 til 55 · Alle køn · Opdateret 9. sep. 2026 · NCT06546670A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease
- Local Institution - 0024, Boston
- Boston Medical Center, Boston
RekruttererFase 1/2Frivillige med god helbredstilstand velkomne
Alder 18 og opefter · Alle køn · Opdateret 18. aug. 2026 · NCT06481306ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
- Massachusetts General Hospital Comprehensive Hemophilia and Thrombosis Treatment Center, Boston
RekruttererObservationsstudie
Alle aldre · Alle køn · Opdateret 17. aug. 2026 · NCT04398628Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease
- Boston Children's Hospital (MRD-HCT), Boston
- Boston Children's Hospital (NT-DMT), Boston
RekruttererObservationsstudie
Alder 3 til 20 · Alle køn · Opdateret 4. jun. 2026 · NCT06941389Promoting Resilience Among Adolescents and Young Adults With Sickle Cell Disease
- Boston Children's Hospital, Boston
Rekrutterer
Alder 8 til 25 · Alle køn · Opdateret 5. maj 2026 · NCT06555939Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies
- Boston Children's Hospital, Boston
RekruttererFase 1
Alder 13 til 40 · Alle køn · Opdateret 3. feb. 2026 · NCT06647979A Long-term Follow-up Study in Patients Who Received BEAM-101
- Boston Children's Hospital, Boston
RekruttererObservationsstudie
Alder 14 til 37 · Alle køn · Opdateret 28. jan. 2026 · NCT07373639A Pilot Study on Neuroimaging in SCD: Part of The Boston Consortium to Cure Sickle Cell Disease
- Boston Children's Hospital, Boston
RekruttererObservationsstudie
Alder 8 til 18 · Alle køn · Opdateret 12. dec. 2025 · NCT04166526Study of the Role of Genetic Modifiers in Hemoglobinopathies
- Boston Children's Hospital, Boston
RekruttererObservationsstudie
Alder 2 og opefter · Alle køn · Opdateret 20. mar. 2024 · NCT05799118Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.