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Spinal muskelatrofi kliniske forsøg i Massachusetts

6 studier for Spinal muskelatrofi søger deltagere på steder i Massachusetts.

Byer i Massachusetts

Officiel studietekst (engelsk)

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Boston Children's Hospital, Boston
RekruttererFase 1
Alder 3 og opefter · Alle køn · Opdateret 3. sep. 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Boston Children's Hospital, Boston
Rekrutterer
Alder 3 og opefter · Alle køn · Opdateret 19. aug. 2026 · NCT05866419

ALS/MND Natural History Study Data Repository

  • Lahey Clinic, Burlington
RekruttererObservationsstudie
Alder 18 til 90 · Alle køn · Opdateret 20. maj 2026 · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Boston Children's Hospital, Boston
RekruttererObservationsstudieFrivillige med god helbredstilstand velkomne
Alder 5 og opefter · Alle køn · Opdateret 9. apr. 2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Boston Children's Hospital, Boston
RekruttererObservationsstudie
Alder 18 til 54 · Kvinder · Opdateret 9. mar. 2026 · NCT05789758

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.