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Spinal muskelatrofi kliniske forsøg i Boston, MA
5 studier for Spinal muskelatrofi søger deltagere på steder i og omkring Boston (inden for ca. 30 miles). Åbn et studie for at se, hvem der kan deltage, og hvordan man kontakter studieteamet.
Officiel studietekst (engelsk)
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A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
RekruttererFase 2
- Boston Children's Hospital, Boston
A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
RekruttererFase 1
- Boston Children's Hospital, Boston
Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
Rekrutterer
- Boston Children's Hospital, Boston
Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
RekruttererObservationsstudieFrivillige med god helbredstilstand velkomne
- Boston Children's Hospital, Boston
A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
RekruttererObservationsstudie
- Boston Children's Hospital, Boston
Spinal muskelatrofi forsøg i andre byer
- Mountain View, CA9 studier
- New York City, NY9 studier
- Philadelphia, PA7 studier
- Chicago, IL6 studier
- Norfolk, VA6 studier
- Grand Rapids, MI6 studier
- Houston, TX5 studier
- Lewisville, TX4 studier
- Little Rock, AR4 studier
- Phoenix, AZ4 studier
- Aurora, CO4 studier
- Memphis, TN3 studier
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Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie har sine egne kvalifikationskrav; studieteamet afgør, hvem der kan deltage.