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Ensayos clínicos de Enfermedad de células falciformes en California

19 estudios sobre Enfermedad de células falciformes buscan participantes en California.

Ciudades en California

Texto oficial del estudio (inglés)

A Phase 1b, Open-Label Study of DISC-3405 in Participants With Sickle Cell Disease (SCD)

  • University of California San Francisco (UCSF) Medical Center, San Francisco
ReclutandoFase 1
Edades de 18 en adelante · Todos los sexos · Actualizado el 13 nov 2026 · NCT07187973

A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

  • Ctr for Inherited Blood Disorders, Orange
ReclutandoFase 3
Edades de 12 a 100 · Todos los sexos · Actualizado el 10 nov 2026 · NCT06439082

HPC Offered for PRESERVE Expansion

  • City of Hope, Duarte
ReclutandoEstudio observacional
Edades de 12 a 80 · Todos los sexos · Actualizado el 6 nov 2026 · NCT07145411

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • University of California Irvine, Orange
ReclutandoFase 2
Edades de 18 en adelante · Todos los sexos · Actualizado el 3 nov 2026 · NCT07224360

Transplantation of Clustered Regularly Interspaced Short Palindromic Repeats Modified Hematopoietic Progenitor Stem Cells (CRISPR_SCD001) in Patients With Severe Sickle Cell Disease

  • University of California, Davis, Davis
  • University of California, Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital, Oakland
ReclutandoFase 1/2
Edades de 12 a 35 · Todos los sexos · Actualizado el 20 oct 2026 · NCT04774536

The Efficacy and Safety of Rilzabrutinib in Participants Aged 10 to 65 Years With Sickle-cell Disease

  • University of California San Francisco- Site Number : 8400040, Clovis
  • David Geffen School of Medicine at UCLA- Site Number : 8400032, Los Angeles
ReclutandoFase 3
Edades de 10 a 65 · Todos los sexos · Actualizado el 15 oct 2026 · NCT06975865

Peer Support for Adolescents and Emerging Adults With Sickle Cell Pain

  • UCLA Mattel Children's Hospital Ronald Reagan Hospital, Los Angeles
Reclutando
Edades de 16 a 39 · Todos los sexos · Actualizado el 8 oct 2026 · NCT06374238

Safety, Efficacy, and Pharmacokinetics of CSL889 in Adults and Adolescents With Sickle Cell Disease During Vaso-Occlusive Crisis

  • Univ. of California, San Francisco Health Care, Oakland
  • University of California Irvine, Orange
ReclutandoFase 2
Edades de 12 en adelante · Todos los sexos · Actualizado el 8 oct 2026 · NCT06699849

Exercise in Child Health

  • University of California, Irvine, Irvine
ReclutandoSe aceptan voluntarios sanos
Edades de 10 a 17 · Todos los sexos · Actualizado el 2 oct 2026 · NCT05359991

A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

  • Children's Hospital Los Angeles - Endocrinology, Los Angeles
  • UCSF Oakland Benioff ChildHosp, Oakland
ReclutandoFase 3
Edades de 2 en adelante · Todos los sexos · Actualizado el 18 sept 2026 · NCT06609226

A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease

  • Children's Hospital Los Angeles - Endocrinology, Los Angeles
  • Valley Children's Hospital, Madera
  • Stanford University_Palo Alto, Palo Alto
  • y 1 más
ReclutandoFase 3
Edades de 12 en adelante · Todos los sexos · Actualizado el 17 sept 2026 · NCT06612268

Sub-dissociative Dose Ketamine in Treatment of Vaso-occlusive Pain Event in Children and Young Adults

  • Harbor UCLA Medical Center, Torrance
ReclutandoFase 2
Edades de 5 a 20 · Todos los sexos · Actualizado el 2 sept 2026 · NCT07369024

A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease

  • University of California San Diego - La Jolla, La Jolla
  • UCSF Benioff Children's Hospital Oakland, Oakland
ReclutandoFase 1/2Se aceptan voluntarios sanos
Edades de 18 en adelante · Todos los sexos · Actualizado el 18 ago 2026 · NCT06481306

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • y 5 más
ReclutandoEstudio observacional
Todas las edades · Todos los sexos · Actualizado el 17 ago 2026 · NCT04398628

Myeloablative Conditioning, Prophylactic Defibrotide and Haplo AlloSCT for Patients With Sickle Cell Disease

  • University of California Los Angeles, Los Angeles
ReclutandoFase 2
6 Months – 21 Years · Todos los sexos · Actualizado el 27 jul 2026 · NCT02675959

Alendronate for Osteonecrosis in Adults With Sickle Cell Disease

  • UC Davis Comprehensive Cancer Center, Sacramento
ReclutandoFase 2
Edades de 18 a 80 · Todos los sexos · Actualizado el 16 jul 2026 · NCT06016634

Gene Correction in Autologous CD34+ Hematopoietic Stem Cells (HbS to HbA) to Treat Severe Sickle Cell Disease

  • Children's Hospital Los Angeles, Los Angeles
  • Lucile Packard Children's Hospital, Palo Alto
ReclutandoFase 1/2
Edades de 12 a 50 · Todos los sexos · Actualizado el 2 jul 2026 · NCT04819841

Zinc Supplementation in Sickle Cell Disease: A Precursor to the Think Zinc for Bones Trial

  • UCSF Benioff Children's Hospital Oakland, Oakland
ReclutandoFase 2
Edades de 15 a 40 · Todos los sexos · Actualizado el 13 mar 2026 · NCT06260891

Recruitment and Engagement in Care to Impact Practice Enhancement (RECIPE) for Sickle Cell Disease

  • University of California, San Francisco (UCSF), Oakland
ReclutandoEstudio observacional
Edades de 18 en adelante · Todos los sexos · Actualizado el 22 jun 2025 · NCT06385886

De ClinicalTrials.gov, datos obtenidos el 15 nov 2026. Cada estudio establece sus propios criterios de elegibilidad; el equipo del estudio decide quién puede participar.