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Ensayos clínicos de Atrofia muscular espinal en California
11 estudios sobre Atrofia muscular espinal buscan participantes en California.
Ciudades en California
Texto oficial del estudio (inglés)
A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- Children's Hospital of Orange County (CHOC), Orange
- Stanford Neuroscience Health Center (SNHC), Palo Alto
ReclutandoFase 2
Hasta los 2 · Todos los sexos · Actualizado el 2 oct 2026 · NCT07047144A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
- Stanford University Medical Center, Palo Alto
ReclutandoFase 3
Edades de 15 a 60 · Todos los sexos · Actualizado el 2 oct 2026 · NCT07444476A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Stanford University Medical Center, Stanford
ReclutandoFase 2
Edades de 5 a 17 · Todos los sexos · Actualizado el 14 sept 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Valley Children's Hospital, Madera
- Stanford Univ Medical Center, Palo Alto
ReclutandoFase 4
3 Months – 24 Months · Todos los sexos · Actualizado el 10 sept 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Children's Hospital of Orange County, Orange
- Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
ReclutandoFase 1
Edades de 3 en adelante · Todos los sexos · Actualizado el 3 sept 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Children's Hospital Orange County, Orange
- Stanford Medical Center, Palo Alto
- Rady Children's Hospital, San Diego
Reclutando
Edades de 3 en adelante · Todos los sexos · Actualizado el 19 ago 2026 · NCT05866419Clinical Procedures to Support Research in ALS
- University of California, Irvine, Irvine
- Stanford University, Palo Alto
- California Pacific Medical Center, San Francisco
ReclutandoEstudio observacional
Edades de 18 en adelante · Todos los sexos · Actualizado el 15 jun 2026 · NCT03489278ALS/MND Natural History Study Data Repository
- Loma Linda University Health, Loma Linda
- Kaiser Permanente, Los Angeles
ReclutandoEstudio observacional
Edades de 18 a 90 · Todos los sexos · Actualizado el 20 may 2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Stanford University, Palo Alto
ReclutandoEstudio observacionalSe aceptan voluntarios sanos
Edades de 5 en adelante · Todos los sexos · Actualizado el 9 abr 2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Stanford Neuroscience Health Center, Palo Alto
ReclutandoEstudio observacional
Edades de 18 a 54 · Mujeres · Actualizado el 9 mar 2026 · NCT05789758Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Children's Hospital of Los Angeles, Los Angeles
- University of California Los Angeles Health, Los Angeles
- Valley Children's Healthcare, Madera
- y 3 más
ReclutandoEstudio observacional
Todas las edades · Todos los sexos · Actualizado el 31 ene 2025 · NCT04174157De ClinicalTrials.gov, datos obtenidos el 5 oct 2026. Cada estudio establece sus propios criterios de elegibilidad; el equipo del estudio decide quién puede participar.