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Ensayos clínicos de Atrofia muscular espinal en California

11 estudios sobre Atrofia muscular espinal buscan participantes en California.

Ciudades en California

Texto oficial del estudio (inglés)

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Hospital of Orange County (CHOC), Orange
  • Stanford Neuroscience Health Center (SNHC), Palo Alto
ReclutandoFase 2
Hasta los 2 · Todos los sexos · Actualizado el 2 oct 2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Valley Children's Hospital, Madera
  • Stanford Univ Medical Center, Palo Alto
ReclutandoFase 4
3 Months – 24 Months · Todos los sexos · Actualizado el 10 sept 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Children's Hospital of Orange County, Orange
  • Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
ReclutandoFase 1
Edades de 3 en adelante · Todos los sexos · Actualizado el 3 sept 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Children's Hospital Orange County, Orange
  • Stanford Medical Center, Palo Alto
  • Rady Children's Hospital, San Diego
Reclutando
Edades de 3 en adelante · Todos los sexos · Actualizado el 19 ago 2026 · NCT05866419

Clinical Procedures to Support Research in ALS

  • University of California, Irvine, Irvine
  • Stanford University, Palo Alto
  • California Pacific Medical Center, San Francisco
ReclutandoEstudio observacional
Edades de 18 en adelante · Todos los sexos · Actualizado el 15 jun 2026 · NCT03489278

ALS/MND Natural History Study Data Repository

  • Loma Linda University Health, Loma Linda
  • Kaiser Permanente, Los Angeles
ReclutandoEstudio observacional
Edades de 18 a 90 · Todos los sexos · Actualizado el 20 may 2026 · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
ReclutandoEstudio observacionalSe aceptan voluntarios sanos
Edades de 5 en adelante · Todos los sexos · Actualizado el 9 abr 2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Stanford Neuroscience Health Center, Palo Alto
ReclutandoEstudio observacional
Edades de 18 a 54 · Mujeres · Actualizado el 9 mar 2026 · NCT05789758

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Children's Hospital of Los Angeles, Los Angeles
  • University of California Los Angeles Health, Los Angeles
  • Valley Children's Healthcare, Madera
  • y 3 más
ReclutandoEstudio observacional
Todas las edades · Todos los sexos · Actualizado el 31 ene 2025 · NCT04174157

De ClinicalTrials.gov, datos obtenidos el 5 oct 2026. Cada estudio establece sus propios criterios de elegibilidad; el equipo del estudio decide quién puede participar.