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Pag-aaral pangklinika para sa beta-Thalassemia na nagre-recruit sa U.S.

15 pag-aaral para sa beta-Thalassemia ang nagre-recruit ng mga kalahok sa mga site sa buong Estados Unidos.

Mga lungsod na may pinakamaraming pag-aaral

Ayos sa estado

Mga pag-aaral na kamakailan lamang in-update

Opisyal na teksto ng pag-aaral (English)

Collection of Human Biospecimens for Basic and Clinical Research Into Globin Variants

Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 18 hanggang 70 · Lahat ng kasarian · Na-update Set 28, 2026 · NCT03937817

ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia

Nagre-recruitPhase 1/2
Edad 18 hanggang 40 · Lahat ng kasarian · Na-update Set 23, 2026 · NCT06364774

Partial Stem Cell Transplant for Sickle Cell Disease From Matched Donors

Nagre-recruitPhase 1/2
Edad 4 hanggang 65 · Lahat ng kasarian · Na-update Set 4, 2026 · NCT07599176

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

Nagre-recruitPhase 1/2
Edad 5 hanggang 40 · Lahat ng kasarian · Na-update Ago 13, 2026 · NCT03653338

Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia

Nagre-recruitPhase 2
Edad 6 hanggang 17 · Lahat ng kasarian · Na-update Hul 10, 2026 · NCT04143724

MT2021-08T Cell Receptor Alpha/Beta Depletion PBSC Transplantation for Heme Malignancies

Nagre-recruitPhase 2
Hanggang edad 60 · Lahat ng kasarian · Na-update Abr 6, 2026 · NCT05735717

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

Nagre-recruitPhase 3
Edad 12 hanggang 35 · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT05477563

Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

Nagre-recruitPhase 1
Edad 13 hanggang 40 · Lahat ng kasarian · Na-update Peb 3, 2026 · NCT06647979

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Nagre-recruitObservasyonal na pag-aaral
2 Months – 60 Years · Lahat ng kasarian · Na-update Ene 13, 2026 · NCT04528355

Study of Panobinostat (LBH589) in Patients With Sickle Cell Disease

Nagre-recruitPhase 1
Edad 18 pataas · Lahat ng kasarian · Na-update Ene 9, 2026 · NCT01245179

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Nagre-recruitPhase 2
2 Months – 55 Years · Lahat ng kasarian · Na-update Dis 15, 2025 · NCT01962415

AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion

Nagre-recruitPhase 2
1 Day – 30 Years · Lahat ng kasarian · Na-update Ago 8, 2025 · NCT04099966

A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Peb 11, 2025 · NCT06271512

Study of the Role of Genetic Modifiers in Hemoglobinopathies

Nagre-recruitObservasyonal na pag-aaral
Edad 2 pataas · Lahat ng kasarian · Na-update Mar 20, 2024 · NCT05799118

Mula sa ClinicalTrials.gov, na-kuha noong Okt 2, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.