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Pag-aaral pangklinika para sa beta-Thalassemia sa New York
5 pag-aaral para sa beta-Thalassemia ang naghahanap ng mga kalahok sa mga site sa New York.
Opisyal na teksto ng pag-aaral (English)
Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia
- New York Presbyterian Hospital, New York
Nagre-recruitPhase 2
Edad 6 hanggang 17 · Lahat ng kasarian · Na-update Hul 10, 2026 · NCT04143724A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT)
- Memorial Sloan Kettering Suffolk - Commack (Consent only), Commack
- Memorial Sloan Kettering Westchester (Consent only), Harrison
- Memorial Sloan Kettering Nassau (All protocol activities), Rockville Centre
Nagre-recruitPhase 2
Edad 2 hanggang 50 · Lahat ng kasarian · Na-update Hun 3, 2026 · NCT05736419Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
- New York Presbyterian Hospital - Morgan Stanley Children's Hospital, New York
Nagre-recruitPhase 3
Edad 12 hanggang 35 · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT05477563AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion
- New York Medical College, Valhalla
Nagre-recruitPhase 2
1 Day – 30 Years · Lahat ng kasarian · Na-update Ago 8, 2025 · NCT04099966A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel
- Cohen Children's Medical Center, New Hyde Park
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Peb 11, 2025 · NCT06271512Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.