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Pag-aaral pangklinika para sa Duchenne Muscular Dystrophy sa Arkansas

7 pag-aaral para sa Duchenne Muscular Dystrophy ang naghahanap ng mga kalahok sa mga site sa Arkansas.

Mga Lungsod sa Arkansas

Opisyal na teksto ng pag-aaral (English)

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

  • Arkansas Children's Hospital, Little Rock
Nagre-recruitPhase 3
Edad 7 hanggang 11 · Kalalakihan · Na-update Set 28, 2026 · NCT07160634

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • Arkansas Children's Hospital, Little Rock
Nagre-recruitPhase 1
Edad 2 pataas · Kalalakihan · Na-update Set 11, 2026 · NCT04626674

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • Arkansas Children's Hospital, Little Rock
Nagre-recruitPhase 1/2
Edad 0 hanggang 17 · Kalalakihan · Na-update Hul 8, 2026 · NCT06138639

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

  • Arkansas Children's Research Institute, Little Rock
Nagre-recruitObservasyonal na pag-aaral
Edad 6 pataas · Lahat ng kasarian · Na-update Hul 2, 2026 · NCT07127978

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

  • Arkansas Children's Hospital, Little Rock
Nagre-recruitPhase 1/2
Edad 2 hanggang 7 · Kalalakihan · Na-update Hun 23, 2026 · NCT07429240

Duchenne Electronic Health Record Study

  • Arkansas Children's Hospital, Little Rock
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update May 27, 2026 · NCT07609394

Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

  • Arkansas Children's Hospital, Little Rock
Nagre-recruitPhase 1/2
Edad 4 hanggang 18 · Kalalakihan · Na-update Dis 15, 2025 · NCT04906460

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.