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Pag-aaral pangklinika para sa Duchenne Muscular Dystrophy na nagre-recruit sa U.S.

26 pag-aaral para sa Duchenne Muscular Dystrophy ang nagre-recruit ng mga kalahok sa mga site sa buong Estados Unidos.

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Opisyal na teksto ng pag-aaral (English)

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

Nagre-recruitPhase 3
Edad 7 hanggang 11 · Kalalakihan · Na-update Set 28, 2026 · NCT07160634

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

Nagre-recruitObservasyonal na pag-aaral
Edad 2 pataas · Kalalakihan · Na-update Set 24, 2026 · NCT06564974

Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy

Nagre-recruitPhase 1
Edad 8 hanggang 18 · Kalalakihan · Na-update Ago 24, 2026 · NCT07172971

The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy

Nagre-recruitObservasyonal na pag-aaral
0 Days – 3 Years · Kalalakihan · Na-update Ago 19, 2026 · NCT07092540

Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients

Nagre-recruit
Edad 6 pataas · Kalalakihan · Na-update Ago 17, 2026 · NCT07766980

Once Weekly Infant Corticosteroid Trial for DMD

Nagre-recruitPhase 4
1 Month – 30 Months · Kalalakihan · Na-update Ago 14, 2026 · NCT05412394

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Hul 28, 2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

Nagre-recruitPhase 1/2
Edad 0 hanggang 17 · Kalalakihan · Na-update Hul 8, 2026 · NCT06138639

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

Nagre-recruitObservasyonal na pag-aaral
Edad 6 pataas · Lahat ng kasarian · Na-update Hul 2, 2026 · NCT07127978

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

Nagre-recruitPhase 1/2
Edad 2 hanggang 7 · Kalalakihan · Na-update Hun 23, 2026 · NCT07429240

Duchenne Electronic Health Record Study

Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update May 27, 2026 · NCT07609394

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD

Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 10 pataas · Kalalakihan · Na-update May 22, 2026 · NCT06124196

Vasodilator and Exercise Study for DMD (VASO-REx)

Nagre-recruitPhase 2
Edad 6 pataas · Kalalakihan · Na-update May 15, 2026 · NCT06290713

The Duchenne Registry

Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update May 8, 2026 · NCT02069756

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Abr 9, 2026 · NCT06839469

Urinary Titin Biomarker in DMD

Nagre-recruitMalugod na tinatanggap ang malusog na boluntaryo
Edad 2 hanggang 10 · Kalalakihan · Na-update Abr 8, 2026 · NCT07332013

Trial of Cell Based Therapy for DMD

Nagre-recruitPhase 1
Edad 18 pataas · Lahat ng kasarian · Na-update Mar 4, 2026 · NCT06692426

Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

Nagre-recruitPhase 1/2
Edad 4 hanggang 18 · Kalalakihan · Na-update Dis 15, 2025 · NCT04906460

Extracellular RNA Biomarkers of Duchenne Muscular Dystrophy

Nagre-recruitObservasyonal na pag-aaral
Edad 5 pataas · Lahat ng kasarian · Na-update Nob 24, 2025 · NCT05016908

Biomarker Development for Muscular Dystrophies

Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Nob 24, 2025 · NCT05019625

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim

Nagre-recruitObservasyonal na pag-aaral
Edad 10 pataas · Kalalakihan · Na-update Nob 6, 2025 · NCT06093100

Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy

Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 hanggang 62 · Kalalakihan · Na-update Okt 15, 2025 · NCT01484678

DMD Voice: Qualitative Interviews With Patients and Caregivers

Nagre-recruitObservasyonal na pag-aaral
Edad 10 pataas · Kalalakihan · Na-update Abr 30, 2025 · NCT06925269

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.