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Pag-aaral pangklinika para sa Duchenne Muscular Dystrophy sa California

6 pag-aaral para sa Duchenne Muscular Dystrophy ang naghahanap ng mga kalahok sa mga site sa California.

Mga Lungsod sa California

Opisyal na teksto ng pag-aaral (English)

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

  • Loma Linda University Pediatric Subspecialty Clinics, Loma Linda
  • Children's Hospital Los Angeles, Los Angeles
  • Valley Children's Hospital, Madera
  • at 2 pa
Nagre-recruitObservasyonal na pag-aaral
Edad 2 pataas · Kalalakihan · Na-update Set 24, 2026 · NCT06564974

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • University of California, San Diego, La Jolla
  • University of California, Los Angeles, Los Angeles
  • Stanford University, Palo Alto
  • at 1 pa
Nagre-recruitPhase 1
Edad 2 pataas · Kalalakihan · Na-update Set 11, 2026 · NCT04626674

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

  • UC Davis, Sacramento
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Hul 28, 2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • University of California, Los Angeles Medical Center, Los Angeles
  • University of California, Davis, Sacramento
  • University of California, San Diego
Nagre-recruitPhase 1/2
Edad 0 hanggang 17 · Kalalakihan · Na-update Hul 8, 2026 · NCT06138639

Duchenne Electronic Health Record Study

  • UC Davis Health, Sacramento
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update May 27, 2026 · NCT07609394

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Abr 9, 2026 · NCT06839469

Mula sa ClinicalTrials.gov, na-kuha noong Okt 6, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.