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Pag-aaral pangklinika para sa Duchenne Muscular Dystrophy sa North Carolina
6 pag-aaral para sa Duchenne Muscular Dystrophy ang naghahanap ng mga kalahok sa mga site sa North Carolina.
Mga Lungsod sa North Carolina
Opisyal na teksto ng pag-aaral (English)
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
- Duke University Medical Center, Durham
Nagre-recruitPhase 1
Edad 2 pataas · Kalalakihan · Na-update Set 11, 2026 · NCT04626674Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials
- Duke Children's Hospital, Durham
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Hul 28, 2026 · NCT07674758A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy
- Duke University / Lenox Baker Children's Hospital, Durham
Nagre-recruitObservasyonal na pag-aaral
Edad 6 pataas · Lahat ng kasarian · Na-update Hul 2, 2026 · NCT07127978Duchenne Electronic Health Record Study
- Duke University Medical Center, Durham
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update May 27, 2026 · NCT07609394Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
- Rare Disease Research, LLC, Hillsborough
Nagre-recruitPhase 3
Edad 4 hanggang 18 · Kalalakihan · Na-update May 27, 2026 · NCT07608432Biomarker Development for Muscular Dystrophies
- Wake Forest University, Winston-Salem
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Nob 24, 2025 · NCT05019625Mula sa ClinicalTrials.gov, na-kuha noong Okt 6, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.