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Pag-aaral pangklinika para sa Friedreich Ataxia na nagre-recruit sa U.S.
13 pag-aaral para sa Friedreich Ataxia ang nagre-recruit ng mga kalahok sa mga site sa buong Estados Unidos.
Mga lungsod na may pinakamaraming pag-aaral
- Tampa, FL4 pag-aaral
- Philadelphia, PA4 pag-aaral
- Los Angeles, CA4 pag-aaral
- New York City, NY3 pag-aaral
- Gainesville, FL3 pag-aaral
Ayos sa estado
Mga pag-aaral na kamakailan lamang in-update
Opisyal na teksto ng pag-aaral (English)
A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
Nagre-recruitPhase 1
Edad 18 hanggang 40 · Lahat ng kasarian · Na-update Set 29, 2026 · NCT07180355Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia
Nagre-recruitPhase 1
Edad 12 hanggang 50 · Lahat ng kasarian · Na-update Set 28, 2026 · NCT05302271Cardiac Output and Fatigue in Friedreich's Ataxia
Nagre-recruit
Lahat ng edad · Lahat ng kasarian · Na-update Set 22, 2026 · NCT07444333An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia
Nagre-recruitPhase 2
Edad 2 hanggang 60 · Lahat ng kasarian · Na-update Set 3, 2026 · NCT06447025Clinical Course Of Disease In Participants With FA-CM
Nagre-recruitObservasyonal na pag-aaral
Edad 6 pataas · Lahat ng kasarian · Na-update Set 2, 2026 · NCT06865482Study of LX2006 Gene Therapy in Friedreich Ataxia Cardiomyopathy
Nagre-recruitPhase 2
Edad 6 pataas · Lahat ng kasarian · Na-update Set 2, 2026 · NCT07721025Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Lahat ng edad · Lahat ng kasarian · Na-update Set 1, 2026 · NCT06016946A Study to Evaluate the Efficacy and Safety of Subcutaneous Nomlabofusp in Subjects With Friedreich's Ataxia
Nagre-recruitPhase 3
Edad 12 hanggang 40 · Lahat ng kasarian · Na-update Ago 31, 2026 · NCT07778836Characterization of the Cardiac Phenotype of Friedreich's Ataxia (FRDA)
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 12 hanggang 50 · Lahat ng kasarian · Na-update Hul 29, 2026 · NCT02316314A Study to Learn How BIIB141 (Omaveloxolone) Affects the Health of Participants With Friedrich's Ataxia Who Took it During Pregnancy and/or During Breastfeeding and About the Health of Their Babies
Nagre-recruitObservasyonal na pag-aaral
Edad 16 pataas · Kababaihan · Na-update Hul 10, 2026 · NCT06628687A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors
Nagre-recruitObservasyonal na pag-aaral
Edad 16 pataas · Lahat ng kasarian · Na-update Abr 28, 2026 · NCT06623890Biomarkers in Friedreich's Ataxia
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 6 hanggang 70 · Lahat ng kasarian · Na-update Set 23, 2025 · NCT02497534Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update May 29, 2025 · NCT01793168Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.