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Pag-aaral pangklinika para sa Genetic Disorders sa Florida

7 pag-aaral para sa Genetic Disorders ang naghahanap ng mga kalahok sa mga site sa Florida.

Mga Lungsod sa Florida

Opisyal na teksto ng pag-aaral (English)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of Miami Miller School of Medicine, Miami
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
1 Month – 100 Years · Lahat ng kasarian · Na-update Set 18, 2026 · NCT02450851

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • University of Florida - Neurology, Gainesville
  • USF Ataxia Research Center, Tampa
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Lahat ng edad · Lahat ng kasarian · Na-update Set 1, 2026 · NCT06016946

A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)

  • GC2501 Study Site 103, Gainesville
  • GC2501 Study Site 105, Miami
Nagre-recruitPhase 3
Edad 18 hanggang 80 · Lahat ng kasarian · Na-update Ago 11, 2026 · NCT07555483

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • The Foundation for Sickle Cell Disease, Hollywood
Nagre-recruitPhase 2
Edad 18 pataas · Lahat ng kasarian · Na-update Ago 5, 2026 · NCT07224360

Rett Syndrome Registry

  • Nicklaus Children's Hospital, Miami
Nagre-recruitObservasyonal na pag-aaral
Edad 0 hanggang 99 · Lahat ng kasarian · Na-update Hun 30, 2026 · NCT05432349

A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)

  • Sirven and Associates, Miami
Nagre-recruitObservasyonal na pag-aaral
Edad 12 pataas · Lahat ng kasarian · Na-update Hun 3, 2026 · NCT07001280

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Nicklaus Children's Hospital, Miami
  • University of South Florida - 12901 Bruce B Downs, Tampa
Nagre-recruitPhase 1/2
Lahat ng edad · Lahat ng kasarian · Na-update Ene 22, 2026 · NCT04159103

Mula sa ClinicalTrials.gov, na-kuha noong Okt 2, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.