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Pag-aaral pangklinika para sa Genetic Disorders sa Ohio
7 pag-aaral para sa Genetic Disorders ang naghahanap ng mga kalahok sa mga site sa Ohio.
Mga Lungsod sa Ohio
Opisyal na teksto ng pag-aaral (English)
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
- Cincinnati Children's Hospital Medical Center, Cincinnati
Nagre-recruitPhase 2/3
Edad 2 hanggang 17 · Lahat ng kasarian · Na-update Set 24, 2026 · NCT07441876Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Ohio State University - Neurology, Columbus
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Lahat ng edad · Lahat ng kasarian · Na-update Set 1, 2026 · NCT06016946A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
- GC2501 Study Site 104, Cleveland
Nagre-recruitPhase 3
Edad 18 hanggang 80 · Lahat ng kasarian · Na-update Ago 11, 2026 · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- Ohio State University, Columbus
Nagre-recruitPhase 2
Edad 18 pataas · Lahat ng kasarian · Na-update Ago 5, 2026 · NCT07224360Prospective Clinical Assessment Study in Children With Hypochondroplasia
- Cincinnati Children's Hospital Medical Center, Cincinnati
Nagre-recruitObservasyonal na pag-aaral
30 Months – 16 Years · Lahat ng kasarian · Na-update Hul 16, 2026 · NCT06410976Rett Syndrome Registry
- Cincinnati Children's Hospital Medical Center, Cincinnati
- Nationwide Children's Hospital, Columbus
Nagre-recruitObservasyonal na pag-aaral
Edad 0 hanggang 99 · Lahat ng kasarian · Na-update Hun 30, 2026 · NCT05432349Helix Research Network
- TriHealth (DNA Discovery), Cincinnati
- The Ohio State University (Genomic Health), Columbus
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 18 pataas · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT06057181Mula sa ClinicalTrials.gov, na-kuha noong Okt 1, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.