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Pag-aaral pangklinika para sa Inborn Errors of Metabolism sa California
5 pag-aaral para sa Inborn Errors of Metabolism ang naghahanap ng mga kalahok sa mga site sa California.
Mga Lungsod sa California
Opisyal na teksto ng pag-aaral (English)
A Long-Term Observational Study of Patients With Fucosidosis
- Children's Hospital of Orange County, Orange
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Set 17, 2026 · NCT07615400Registry of Patients Diagnosed With Lysosomal Storage Diseases
- University of California San Francisco, San Francisco
Nagre-recruitObservasyonal na pag-aaral
Hanggang edad 64 · Lahat ng kasarian · Na-update Abr 8, 2026 · NCT05619900A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- Ronald Reagan UCLA Medical Center, Los Angeles
- University of Stanford Medical Center, Palo Alto
Nagre-recruitPhase 1/2
Edad 1 pataas · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT05130437Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
- Ronald Reagan UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital Stanford, Stanford
Nagre-recruitPhase 1/2
Lahat ng edad · Lahat ng kasarian · Na-update Ene 22, 2026 · NCT04159103An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
- UCLA Medical Center, Los Angeles
- Lucile Packard Children's Hospital at Stanford, Palo Alto
- Altman Clinical and Translational Research Institution, San Diego
Nagre-recruitPhase 1/2
Edad 1 pataas · Lahat ng kasarian · Na-update Dis 23, 2025 · NCT05295433Mula sa ClinicalTrials.gov, na-kuha noong Okt 1, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.