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Pag-aaral pangklinika para sa Inborn Errors of Metabolism sa California

5 pag-aaral para sa Inborn Errors of Metabolism ang naghahanap ng mga kalahok sa mga site sa California.

Mga Lungsod sa California

Opisyal na teksto ng pag-aaral (English)

A Long-Term Observational Study of Patients With Fucosidosis

  • Children's Hospital of Orange County, Orange
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Set 17, 2026 · NCT07615400

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
Nagre-recruitObservasyonal na pag-aaral
Hanggang edad 64 · Lahat ng kasarian · Na-update Abr 8, 2026 · NCT05619900

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Ronald Reagan UCLA Medical Center, Los Angeles
  • University of Stanford Medical Center, Palo Alto
Nagre-recruitPhase 1/2
Edad 1 pataas · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT05130437

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
  • Ronald Reagan UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital Stanford, Stanford
Nagre-recruitPhase 1/2
Lahat ng edad · Lahat ng kasarian · Na-update Ene 22, 2026 · NCT04159103

An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705

  • UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital at Stanford, Palo Alto
  • Altman Clinical and Translational Research Institution, San Diego
Nagre-recruitPhase 1/2
Edad 1 pataas · Lahat ng kasarian · Na-update Dis 23, 2025 · NCT05295433

Mula sa ClinicalTrials.gov, na-kuha noong Okt 1, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.