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Pag-aaral pangklinika para sa Inborn Errors of Metabolism na nagre-recruit sa U.S.
12 pag-aaral para sa Inborn Errors of Metabolism ang nagre-recruit ng mga kalahok sa mga site sa buong Estados Unidos.
Mga lungsod na may pinakamaraming pag-aaral
- Philadelphia, PA4 pag-aaral
- Washington, DC3 pag-aaral
- Los Angeles, CA3 pag-aaral
- New York City, NY3 pag-aaral
- Mountain View, CA3 pag-aaral
Ayos sa estado
Mga pag-aaral na kamakailan lamang in-update
Opisyal na teksto ng pag-aaral (English)
Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
1 Month – 100 Years · Lahat ng kasarian · Na-update Nob 12, 2026 · NCT02890342Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
Nagre-recruitObservasyonal na pag-aaral
7 Months – 15 Months · Lahat ng kasarian · Na-update Nob 5, 2026 · NCT06805695Clinical and Laboratory Study of Methylmalonic Acidemia
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
1 Month – 115 Years · Lahat ng kasarian · Na-update Okt 29, 2026 · NCT00078078Study of Zodasiran in Adolescent Participants With Homozygous Familial Hypercholesterolemia
Nagre-recruitPhase 3
Edad 12 hanggang 17 · Lahat ng kasarian · Na-update Okt 26, 2026 · NCT07473843Study of Alkaptonuria
Nagre-recruitObservasyonal na pag-aaral
Edad 2 hanggang 115 · Lahat ng kasarian · Na-update Okt 16, 2026 · NCT00005909A Long-Term Observational Study of Patients With Fucosidosis
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Set 17, 2026 · NCT07615400Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT
Nagre-recruitPhase 1/2
1 Month – 25 Years · Lahat ng kasarian · Na-update Abr 15, 2026 · NCT06839456Registry of Patients Diagnosed With Lysosomal Storage Diseases
Nagre-recruitObservasyonal na pag-aaral
Hanggang edad 64 · Lahat ng kasarian · Na-update Abr 8, 2026 · NCT05619900A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
Nagre-recruitPhase 1/2
Edad 1 pataas · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT05130437Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC
Nagre-recruitMaagang Phase 1
Hanggang edad 30 · Lahat ng kasarian · Na-update Peb 20, 2026 · NCT02356653Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
Nagre-recruitPhase 1/2
Lahat ng edad · Lahat ng kasarian · Na-update Ene 22, 2026 · NCT04159103An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
Nagre-recruitPhase 1/2
Edad 1 pataas · Lahat ng kasarian · Na-update Dis 23, 2025 · NCT05295433Mula sa ClinicalTrials.gov, na-kuha noong Nob 15, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.