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Pag-aaral pangklinika para sa Inborn Errors of Metabolism sa Pennsylvania

6 pag-aaral para sa Inborn Errors of Metabolism ang naghahanap ng mga kalahok sa mga site sa Pennsylvania.

Mga Lungsod sa Pennsylvania

Opisyal na teksto ng pag-aaral (English)

Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

  • Children's Hospital of Pittsburgh, Pittsburgh
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
1 Month – 100 Years · Lahat ng kasarian · Na-update Set 28, 2026 · NCT02890342

Clinical and Laboratory Study of Methylmalonic Acidemia

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
1 Month – 115 Years · Lahat ng kasarian · Na-update Set 10, 2026 · NCT00078078

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

  • Children's Hospital of Philadelphia, Philadelphia
Nagre-recruitPhase 1/2
1 Month – 25 Years · Lahat ng kasarian · Na-update Abr 15, 2026 · NCT06839456

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
Nagre-recruitPhase 1/2
Edad 1 pataas · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT05130437

Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC

  • Children's Hospital of Philadelphia, Philadelphia
Nagre-recruitMaagang Phase 1
Hanggang edad 30 · Lahat ng kasarian · Na-update Peb 20, 2026 · NCT02356653

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Nagre-recruitPhase 1/2
Lahat ng edad · Lahat ng kasarian · Na-update Ene 22, 2026 · NCT04159103

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.