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Pag-aaral pangklinika para sa Myotonic Dystrophy sa Florida
4 pag-aaral para sa Myotonic Dystrophy ang naghahanap ng mga kalahok sa mga site sa Florida.
Mga Lungsod sa Florida
Opisyal na teksto ng pag-aaral (English)
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- UF Health: University of Florida Clinical Research Center, Gainesville
Nagre-recruitPhase 3
Edad 16 pataas · Lahat ng kasarian · Na-update Nob 13, 2026 · NCT07486934Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- University of Florida, Gainesville
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 70 · Lahat ng kasarian · Na-update Nob 3, 2026 · NCT03981575A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- University of Florida, 2004 Mowry Road - Site Number: 8400005, Gainesville
- University of South Florida - Neuromuscular Research, 13330 USF Laurel Drive - Site Number: 8400001, Tampa
Nagre-recruitPhase 1/2
Edad 10 hanggang 55 · Lahat ng kasarian · Na-update Set 21, 2026 · NCT06844214Study of ATX-01 in Participants With DM1
- University of Florida, Gainesville
Nagre-recruitPhase 1/2
Edad 18 hanggang 64 · Lahat ng kasarian · Na-update Peb 10, 2026 · NCT06300307Mula sa ClinicalTrials.gov, na-kuha noong Nob 15, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.