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Pag-aaral pangklinika para sa Myotonic Dystrophy na nagre-recruit sa U.S.
19 pag-aaral para sa Myotonic Dystrophy ang nagre-recruit ng mga kalahok sa mga site sa buong Estados Unidos.
Mga lungsod na may pinakamaraming pag-aaral
- Richmond, VA8 pag-aaral
- Rochester, NY7 pag-aaral
- Boston, MA4 pag-aaral
- Los Angeles, CA4 pag-aaral
- Cedar Rapids, IA3 pag-aaral
- Gainesville, FL3 pag-aaral
Ayos sa estado
- California5 pag-aaral
- Florida3 pag-aaral
- Iowa3 pag-aaral
- Kansas4 pag-aaral
- Massachusetts4 pag-aaral
- New York8 pag-aaral
- North Carolina4 pag-aaral
- Pennsylvania3 pag-aaral
- Texas3 pag-aaral
- Virginia8 pag-aaral
Mga pag-aaral na kamakailan lamang in-update
Opisyal na teksto ng pag-aaral (English)
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
Nagre-recruitPhase 3
Edad 16 pataas · Lahat ng kasarian · Na-update Set 25, 2026 · NCT07486934A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
Nagre-recruitPhase 1/2
Edad 10 hanggang 55 · Lahat ng kasarian · Na-update Set 21, 2026 · NCT06844214Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 70 · Lahat ng kasarian · Na-update Set 4, 2026 · NCT07700225Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
Nagre-recruitObservasyonal na pag-aaral
Edad 3 hanggang 17 · Lahat ng kasarian · Na-update Ago 11, 2026 · NCT06747884DMCRN-02-001: Assessing Pediatric Endpoints in DM1
Nagre-recruitObservasyonal na pag-aaral
59 Months · Lahat ng kasarian · Na-update Hun 10, 2026 · NCT05224778Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 70 · Lahat ng kasarian · Na-update Hun 10, 2026 · NCT03981575Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy
Nagre-recruitObservasyonal na pag-aaral
Edad 0 hanggang 17 · Lahat ng kasarian · Na-update Hun 5, 2026 · NCT07630389Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
Nagre-recruitPhase 3
Edad 4 hanggang 18 · Kalalakihan · Na-update May 27, 2026 · NCT07608432Investigating Exercise in Myotonic Dystrophy Type 2 (DM2)
Nagre-recruit
Edad 18 hanggang 70 · Lahat ng kasarian · Na-update Abr 15, 2026 · NCT06716931Remote Assessments and Genetic Determinants of Myotonic Dystrophy
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 88 · Lahat ng kasarian · Na-update Abr 1, 2026 · NCT07505342Study of ATX-01 in Participants With DM1
Nagre-recruitPhase 1/2
Edad 18 hanggang 64 · Lahat ng kasarian · Na-update Peb 10, 2026 · NCT06300307Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 18 hanggang 65 · Lahat ng kasarian · Na-update Ene 23, 2026 · NCT07362875Biomarker Development for Muscular Dystrophies
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Nob 24, 2025 · NCT05019625Extracellular RNA Biomarkers of Myotonic Dystrophy
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Nob 24, 2025 · NCT05020002Cerebrospinal Fluid Biomarkers of Myotonic Dystrophy
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Nob 24, 2025 · NCT06075693Long-Term Development of Muscular Dystrophy Outcome Assessments
Nagre-recruitObservasyonal na pag-aaral
Edad 6 hanggang 50 · Lahat ng kasarian · Na-update Nob 18, 2025 · NCT05989620Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Lahat ng edad · Lahat ng kasarian · Na-update Okt 15, 2025 · NCT00082108Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
Nagre-recruitPhase 2/3
Edad 6 hanggang 45 · Lahat ng kasarian · Na-update May 28, 2025 · NCT05004129Myotonic Dystrophy Family Registry
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Nob 21, 2024 · NCT02398786Mula sa ClinicalTrials.gov, na-kuha noong Set 30, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.