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Pag-aaral pangklinika para sa Myotonic Dystrophy sa New York
8 pag-aaral para sa Myotonic Dystrophy ang naghahanap ng mga kalahok sa mga site sa New York.
Mga Lungsod sa New York
Opisyal na teksto ng pag-aaral (English)
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- University of Rochester Medical Center, Rochester
Nagre-recruitPhase 3
Edad 16 pataas · Lahat ng kasarian · Na-update Nob 13, 2026 · NCT07486934DMCRN-02-001: Assessing Pediatric Endpoints in DM1
- University of Rochester Medical Center, Rochester
Nagre-recruitObservasyonal na pag-aaral
59 Months · Lahat ng kasarian · Na-update Nob 3, 2026 · NCT05224778Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
- University of Rochester, Rochester
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 70 · Lahat ng kasarian · Na-update Nob 3, 2026 · NCT03981575A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
- Columbia University Medical Center - Neurological Institute, 710 W. 168th, 2nd floor, suite 204 - Site Number : 8400003, New York
Nagre-recruitPhase 1/2
Edad 10 hanggang 55 · Lahat ng kasarian · Na-update Set 21, 2026 · NCT06844214Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy
- University of Rochester, Rochester
Nagre-recruitObservasyonal na pag-aaral
Edad 0 hanggang 17 · Lahat ng kasarian · Na-update Hun 5, 2026 · NCT07630389Remote Assessments and Genetic Determinants of Myotonic Dystrophy
- University of Rochester, Rochester
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 88 · Lahat ng kasarian · Na-update Abr 1, 2026 · NCT07505342Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
- University of Rochester Medical Center, Department of Neurology, Rochester
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Lahat ng edad · Lahat ng kasarian · Na-update Okt 15, 2025 · NCT00082108Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
- University of Rochester - Medical Center, Rochester
Nagre-recruitPhase 2/3
Edad 6 hanggang 45 · Lahat ng kasarian · Na-update May 28, 2025 · NCT05004129Mula sa ClinicalTrials.gov, na-kuha noong Nob 15, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.