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Pag-aaral pangklinika para sa Myotonic Dystrophy sa Virginia

8 pag-aaral para sa Myotonic Dystrophy ang naghahanap ng mga kalahok sa mga site sa Virginia.

Mga Lungsod sa Virginia

Opisyal na teksto ng pag-aaral (English)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • Virginia Commonwealth University - Biotech One, Richmond
Nagre-recruitPhase 3
Edad 16 pataas · Lahat ng kasarian · Na-update Okt 1, 2026 · NCT07486934

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

  • Virginia Commonwealth University Medical Center- Site Number : 8400006, Richmond
Nagre-recruitPhase 1/2
Edad 10 hanggang 55 · Lahat ng kasarian · Na-update Set 21, 2026 · NCT06844214

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

  • Virginia Commonwealth University, Richmond
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 70 · Lahat ng kasarian · Na-update Set 4, 2026 · NCT07700225

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

  • Virginia Commonwealth University, Richmond
Nagre-recruitObservasyonal na pag-aaral
Edad 3 hanggang 17 · Lahat ng kasarian · Na-update Ago 11, 2026 · NCT06747884

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

  • Virginia Commonwealth University, Richmond
Nagre-recruitObservasyonal na pag-aaral
59 Months · Lahat ng kasarian · Na-update Hun 10, 2026 · NCT05224778

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

  • Virginia Commonwealth University, Richmond
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 70 · Lahat ng kasarian · Na-update Hun 10, 2026 · NCT03981575

Study of ATX-01 in Participants With DM1

  • Virginia Commonwealth University, Richmond
Nagre-recruitPhase 1/2
Edad 18 hanggang 64 · Lahat ng kasarian · Na-update Peb 10, 2026 · NCT06300307

Long-Term Development of Muscular Dystrophy Outcome Assessments

  • Virginia Commonwealth University, Richmond
Nagre-recruitObservasyonal na pag-aaral
Edad 6 hanggang 50 · Lahat ng kasarian · Na-update Nob 18, 2025 · NCT05989620

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.